2
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Cardioneuromyopathy with hyaline masses and nemaline rods | Survanta intratracheal suspension | Orphan Designation | - |
| Frank-Ter Haar syndrome | Beractant | Orphan Designation | - |
| RD3-related retinopathy | Survanta intratracheal suspension | Orphan Designation | - |
| adult acute respiratory distress syndrome | Survanta intratracheal suspension | Orphan Designation | - |
| fountain syndrome | Beractant | Orphan Designation | - |
| idiopathic non-lupus full-house nephropathy | Beractant | Orphan Designation | - |
| newborn respiratory distress syndrome | Survanta intratracheal suspension | Orphan Designation | - |
| respiratory distress syndrome in premature infants | Survanta intratracheal suspension | Orphan Designation | - |