2
Orphan Designations
0
FDA Approvals
2
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| malignant glioma | 8-((6-iodobenzo[d][1,3]dioxol-5-yl)thio)-9-(2-(neopentylamino)ethyl)-9H-purin-6-amine, dihydrochloride salt | Orphan Designation | - |
| myelofibrosis | 8-(6-iodobenzo[1,3]dioxol-5-ylsufanyl)-9-(3-isopropylamino propyl)adenine dihydrochloride | Orphan Designation | - |