4
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute flaccid myelitis | ST1-RTA immunotoxin (SR 44163) | Orphan Designation | - |
| acute graft versus host disease | ST1-RTA immunotoxin (SR 44163) | Orphan Designation | - |
| acute lymphoblastic leukemia | ST1-RTA immunotoxin (SR 44163) | Orphan Designation | - |
| cystic kidney disease | Succimer | Orphan Designation | - |
| juvenile nephropathic cystinosis | Succimer | Orphan Designation | - |
| mercury poisoning | Succimer | Orphan Designation | - |
| nephropathic cystinosis | Succimer | Orphan Designation | - |
| pneumocystosis | Primaquine phosphate | Orphan Designation | - |