1
Orphan Designations
1
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| chronic graft versus host disease | sirolimus | Orphan Designation | - |
| chronic inflammatory demyelinating polyradiculoneuropathy | sirolimus | Orphan Designation | - |
| chronic primary adrenal insufficiency | sirolimus | Orphan Designation | - |
| chronic recurrent multifocal osteomyelitis | sirolimus | Orphan Designation | - |
| developmental and epileptic encephalopathy 98 | sirolimus | Orphan Designation | - |
| non-infectious anterior uveitis | sirolimus | Orphan Designation | - |