1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Blount disease, adolescent | dexrazoxane hydrochloride | Orphan Designation | - |
| adolescent idiopathic scoliosis | dexrazoxane hydrochloride | Orphan Designation | - |
| autosomal dominant epilepsy with auditory features | dexrazoxane hydrochloride | Orphan Designation | - |
| benign focal seizures of adolescence | dexrazoxane hydrochloride | Orphan Designation | - |
| cartilage-hair hypoplasia | dexrazoxane hydrochloride | Orphan Designation | - |
| cramps, familial adolescent | dexrazoxane hydrochloride | Orphan Designation | - |