8
Orphan Designations
0
FDA Approvals
7
Rare Diseases
1
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| bronchiectasis | ciprofloxacinLiposomal ciprofloxacin for inhalation | Orphan Designation | - |
| cystic fibrosis | liposomal ciprofloxacin plus ciprofloxacingranulocyte macrophage colony stimuling factorliposomal ciprofloxacin for inhalation | Orphan Designation | - |
| diffuse alveolar hemorrhage | Recombinant coagulation factor VIIa | Orphan Designation | - |
| persistent fetal circulation syndrome | vancomycin hydrochloride (inhalational) | Orphan Designation | - |
| persistent hyperplastic primary vitreous | vancomycin hydrochloride (inhalational) | Orphan Designation | - |
| persistent idiopathic facial pain | vancomycin hydrochloride (inhalational) | Orphan Designation | - |
| pulmonary alveolar proteinosis | recombinant human GM-CSF, molgramostim | Orphan Designation | - |