19
Orphan Designations
0
FDA Approvals
35
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| AIDS | Molgramostim | Orphan Designation | - |
| AIDS dementia complex | Intron A | Orphan Designation | - |
| AIDS dysmorphic syndrome | Molgramostim | Orphan Designation | - |
| AIDS related complex | MolgramostimIntron A | Orphan Designation | - |
| AIDS-related disorder | Intron A | Orphan Designation | - |
| African iron overload | REBETOL | Orphan Designation | - |
| Kaposi's sarcoma | Intron A | Orphan Designation | - |
| Sjogren syndrome | REBETOL | Orphan Designation | - |
| acute hepatitis B virus infection | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| aplastic anemia | Molgramostim | Orphan Designation | - |
| atypical teratoid rhabdoid tumor | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| bladder carcinoma in situ | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| brain cancer | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| brainstem cancer | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| breast carcinoma in situ | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| chronic hepatitis C virus infection | REBETOL | Orphan Designation | - |
| chronic myelogenous leukemia, BCR-ABL1 positive | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| clear cell renal carcinoma | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| ectodermal dysplasia syndrome | Intron A | Orphan Designation | - |
| hepatitis C virus infection | REBETOL | Orphan Designation | - |
| invasive breast carcinoma | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| laryngeal abductor paralysis | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| metastatic malignant neoplasm in the colon | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| metastatic melanoma | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| myelodysplastic syndrome | Granulocyte macrophage-colony stimulating factor | Orphan Designation | - |
| neutropenia | Granulocyte macrophage-colony stimulating factor | Orphan Designation | - |
| non-invasive verrucous carcinoma of the penis | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| ovarian cancer | Recombinant replication deficient adenovirus vector carrying human p53 gene | Orphan Designation | - |
| ovarian carcinoma | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| recurrent respiratory papillomatosis | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| respiratory papillomatosis, juvenile recurrent, congenital | Interferon alfa-2b (recombinant) | Orphan Designation | - |
| severe Canavan disease | Granulocyte macrophage-colony stimulating factor | Orphan Designation | - |
| severe achondroplasia-developmental delay-acanthosis nigricans syndrome | Granulocyte macrophage-colony stimulating factor | Orphan Designation | - |
| severe intellectual disability-poor language-strabismus-grimacing face-long fingers syndrome | Granulocyte macrophage-colony stimulating factor | Orphan Designation | - |
| somatostatinoma | Interferon alfa-2b (recombinant) | Orphan Designation | - |