2
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Down syndrome | Anaritide acetate | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | Anaritide acetate | Orphan Designation | - |
| multiple congenital anomalies-hypotonia-seizures syndrome 2 | Anaritide acetate | Orphan Designation | - |