4
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| biliary tract cancer | Silmitasertib | Orphan Designation | - |
| cholangiocarcinoma | Silmitasertib | Orphan Designation | - |
| medulloblastoma | silmitasertib | Orphan Designation | - |
| neuroblastoma | silmitasertib | Orphan Designation | - |