1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| neurodevelopmental disorder with hypotonia, feeding difficulties, facial dysmorphism, and brain abnormalities | bentracimab | Orphan Designation | - |
| neurodevelopmental disorder with intracranial hemorrhage, seizures, and spasticity | bentracimab | Orphan Designation | - |
| neurodevelopmental disorder with spasticity and poor growth | bentracimab | Orphan Designation | - |