1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| PENS syndrome | patidegib | Orphan Designation | - |
| linear and whorled nevoid hypermelanosis | patidegib | Orphan Designation | - |
| nevoid basal cell carcinoma syndrome | patidegib | Orphan Designation | - |