2
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| homozygous familial hypercholesterolemia | Sodium dichloroacetate | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 13 | Sodium dichloroacetate | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 9 | Sodium dichloroacetate | Orphan Designation | - |