Kisho

SuperGen, Inc. — Rare Disease Pipeline | Kisho | Kisho

SuperGen, Inc.

Other

Orphan Designations

FDA Approvals

Rare Diseases

News Articles

Disease	Drug(s)	Designation	Approved
AIDS	rubitecan	Orphan Designation	-
Fanconi anemia complementation group F	Nipent	Orphan Designation	-
Prader-Willi syndrome	Etiocholanedione	Orphan Designation	-
Sezary syndrome	Pentostatin	Orphan Designation	-
acute leukemia	5-aza-2'-deoxycytidine	Orphan Designation	-
aplastic anemia	Etiocholanedione	Orphan Designation	-
brain sarcoma	Busulfan	Orphan Designation	-
congenital lethal erythroderma	4-[1]benzofuro[3,2-d]pyrimidin-4-yl-N-(1,3-benzodioxol-5-ylmethyl)piperazine-1-carbothioamide	Orphan Designation	-
enteropathy-associated T-cell lymphoma	Pentostatin	Orphan Designation	-
giant cell reparative granuloma	busulfan	Orphan Designation	-
hairy cell leukemia	Nipent	Orphan Designation	-
intestinal pseudoobstruction, neuronal, chronic idiopathic, X-linked	Pentostatin	Orphan Designation	-
major depressive disorder	4-[1]benzofuro[3,2-d]pyrimidin-4-yl-N-(1,3-benzodioxol-5-ylmethyl)piperazine-1-carbothioamide	Orphan Designation	-
malignant pancreatic neoplasm	9-nitro-20-(S)-camptothecin	Orphan Designation	-
mitochondrial DNA depletion syndrome 13	Pentostatin	Orphan Designation	-
pediatric acute-onset neuropsychiatric syndrome	rubitecan	Orphan Designation	-
pediatric hepatocellular carcinoma	rubitecan	Orphan Designation	-
pediatric ovarian dysgerminoma	rubitecan	Orphan Designation	-
pediatric ovarian germ cell tumor	rubitecan	Orphan Designation	-
pediatric-onset Graves disease	rubitecan	Orphan Designation	-
peroxisomal single enzyme/protein defect	Nipent	Orphan Designation	-
post 5-alpha-reductase inhibitors treatment syndrome	4-[1]benzofuro[3,2-d]pyrimidin-4-yl-N-(1,3-benzodioxol-5-ylmethyl)piperazine-1-carbothioamide	Orphan Designation	-
post-treatment Lyme disease syndrome	4-[1]benzofuro[3,2-d]pyrimidin-4-yl-N-(1,3-benzodioxol-5-ylmethyl)piperazine-1-carbothioamide	Orphan Designation	-
primary brain neoplasm	Busulfan	Orphan Designation	-
primary central nervous system lymphoma	Busulfan	Orphan Designation	-
primary cutaneous T-cell non-Hodgkin lymphoma	Pentostatin	Orphan Designation	-
rhizomelic limb shortening with dysmorphic features	Pentostatin	Orphan Designation	-
secondary dentine	busulfan	Orphan Designation	-
single isolated optic neuritis	Nipent	Orphan Designation	-
single-organ polyarteritis nodosa	Nipent	Orphan Designation	-
single-system multifocal langerhans cell histiocytosis	Nipent	Orphan Designation	-
treatment-refractory schizophrenia	4-[1]benzofuro[3,2-d]pyrimidin-4-yl-N-(1,3-benzodioxol-5-ylmethyl)piperazine-1-carbothioamide	Orphan Designation	-

← Back to Companies