2
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| cancer-associated retinopathy | autologous human peripheral blood mononuclear cells incubated ex vivo with protein TBX-4000 (Tat-MYC) | Orphan Designation | - |
| cutaneous melanoma | autologous human peripheral blood mononuclear cells incubated ex vivo with protein TBX-4000 (Tat-MYC) | Orphan Designation | - |
| epilepsy, familial adult myoclonic, 2 | human donor hematopoietic stem and progenitor cells (HSPC) that have been treated ex vivo with TBX-4000 | Orphan Designation | - |
| epilepsy, familial adult myoclonic, 3 | human donor hematopoietic stem and progenitor cells (HSPC) that have been treated ex vivo with TBX-4000 | Orphan Designation | - |
| epilepsy, familial adult myoclonic, 4 | human donor hematopoietic stem and progenitor cells (HSPC) that have been treated ex vivo with TBX-4000 | Orphan Designation | - |
| malignant cornea melanoma | autologous human peripheral blood mononuclear cells incubated ex vivo with protein TBX-4000 (Tat-MYC) | Orphan Designation | - |