1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| mercury poisoning | 20-alphaHydroxycholesterol | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 6 (hepatocerebral type) | 20-alphaHydroxycholesterol | Orphan Designation | - |
| pseudo-TORCH syndrome 3 | 20-alphaHydroxycholesterol | Orphan Designation | - |