1
Orphan Designations
6
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Cowden syndrome 1 | Xermelo | Orphan Designation | - |
| Cowden syndrome 6 | Xermelo | Orphan Designation | - |
| Cowden syndrome 7 | Xermelo | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 6 (hepatocerebral type) | Xermelo | Orphan Designation | - |