1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Kabuki syndrome 1 | poly-N,N'-hexamethyleneguanidine-poly-N1,N4-hexamethyleneaminoguanidine | Orphan Designation | - |
| congenital total pulmonary venous return anomaly | poly-N,N'-hexamethyleneguanidine-poly-N1,N4-hexamethyleneaminoguanidine | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 13 | poly-N,N'-hexamethyleneguanidine-poly-N1,N4-hexamethyleneaminoguanidine | Orphan Designation | - |