1
Orphan Designations
2
FDA Approvals
10
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| 8p inverted duplication/deletion syndrome | Trogarzo | Orphan Designation | - |
| Kabuki syndrome 1 | Trogarzo | Orphan Designation | - |
| Richieri Costa-Pereira syndrome | Trogarzo | Orphan Designation | - |
| Singleton-Merten syndrome 1 | Trogarzo | Orphan Designation | - |
| chromosome 16p13.3 duplication syndrome | Trogarzo | Orphan Designation | - |
| cleidocranial dysplasia 1 | Trogarzo | Orphan Designation | - |
| congenital human immunodeficiency virus | Trogarzo | Orphan Designation | - |
| ectodermal dysplasia 17 with or without limb malformations | Trogarzo | Orphan Designation | - |
| intellectual disability, autosomal dominant 1 | Trogarzo | Orphan Designation | - |
| symphalangism with multiple anomalies of hands and feet | Trogarzo | Orphan Designation | - |