3
Orphan Designations
0
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute intermittent porphyria | Anti-T cell receptor murine monoclonal antibody | Orphan Designation | - |
| acute stress disorder | Anti-T cell receptor murine monoclonal antibody | Orphan Designation | - |
| intellectual disability, autosomal dominant 16 | anti-TCR murine monoclonal antibody (MAb, type IgM) | Orphan Designation | - |
| long QT syndrome 16 | anti-TCR murine monoclonal antibody (MAb, type IgM) | Orphan Designation | - |
| nephronophthisis 16 | anti-TCR murine monoclonal antibody (MAb, type IgM) | Orphan Designation | - |
| pediatric hepatocellular carcinoma | anti-TCR murine monoclonal antibody (MAB, type IgM) | Orphan Designation | - |
| pediatric multiple sclerosis | anti-TCR murine monoclonal antibody (MAB, type IgM) | Orphan Designation | - |
| pediatric-onset Graves disease | anti-TCR murine monoclonal antibody (MAB, type IgM) | Orphan Designation | - |
| yellow fever | Anti-T cell receptor murine monoclonal antibody | Orphan Designation | - |