2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| mitochondrial DNA depletion syndrome 13 | Sodium phenylacetate/sodium benzoate 10%/10% Injection | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 9 | Sodium phenylacetate/sodium benzoate 10%/10% Injection | Orphan Designation | - |
| spinal muscular atrophy | Glyceryl tri (4-phenylbutyrate) | Orphan Designation | - |
| tumor grade 3, general grading system | Sodium phenylacetate/sodium benzoate 10%/10% Injection | Orphan Designation | - |