1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| carbon monoxide-induced delayed encephalopathy | (S)-1-((((1-Cyclohexylethyl)carbamoyl)oxy)methyl)-3-((2- nitrooxy)ethyl)carbamoyl)pyridin-1-ium iodide | Orphan Designation | - |
| delayed membranous cranial ossification | (S)-1-((((1-Cyclohexylethyl)carbamoyl)oxy)methyl)-3-((2- nitrooxy)ethyl)carbamoyl)pyridin-1-ium iodide | Orphan Designation | - |
| delayed puberty, self-limited | (S)-1-((((1-Cyclohexylethyl)carbamoyl)oxy)methyl)-3-((2- nitrooxy)ethyl)carbamoyl)pyridin-1-ium iodide | Orphan Designation | - |