1
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| DYRK1A-related intellectual disability syndrome | Iobenguane Sulfate I 131 | Orphan Designation | - |
| anosmia for isobutyric acid | Iobenguane Sulfate I 131 | Orphan Designation | - |
| double nail for fifth toe | Iobenguane Sulfate I 131 | Orphan Designation | - |
| neuroacanthocytosis | Iobenguane Sulfate I 131 | Orphan Designation | - |