3
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Renpenning syndrome | Purified Human Allogeneic Pancreatic Islets of Langerhans | Orphan Designation | - |
| acute flaccid myelitis | Urinary-derived human chorionic gonadotropin and epidermal growth factor | Orphan Designation | - |
| acute graft versus host disease | Urinary-derived human chorionic gonadotropin and epidermal growth factor | Orphan Designation | - |
| acute lymphoblastic leukemia | Urinary-derived human chorionic gonadotropin and epidermal growth factor | Orphan Designation | - |
| brittle cornea syndrome | Purified Human Allogeneic Pancreatic Islets of Langerhans | Orphan Designation | - |
| malignant pancreatic neoplasm | infectivity-enhanced, COX2 promoter-controlled oncolytic adenovirus | Orphan Designation | - |
| orofaciodigital syndrome I | Purified Human Allogeneic Pancreatic Islets of Langerhans | Orphan Designation | - |