1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Bailey-Bloch congenital myopathy | Epoprostenol | Orphan Designation | - |
| myopathy, distal, 7, adult-onset, X-linked | Epoprostenol | Orphan Designation | - |
| myopathy, myofibrillar, 13, with rimmed vacuoles | Epoprostenol | Orphan Designation | - |