5
Orphan Designations
0
FDA Approvals
13
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| carbon monoxide-induced delayed encephalopathy | angiotensin (1-7) | Orphan Designation | - |
| cerebrospinal fluid leak | NorLeu3-Angiontensin(1-7)) [NorLeu3-A(1-7)] | Orphan Designation | - |
| congenital total pulmonary venous return anomaly | angiotensin (1-7) | Orphan Designation | - |
| dermal Ridges, patternless | NorLeu3-Angiotensin(1-7) [NorLeu3-A(1-7)] | Orphan Designation | - |
| dermal unilateral segmental cavernous angioma | NorLeu3-Angiotensin(1-7) [NorLeu3-A(1-7)] | Orphan Designation | - |
| granulomatosis with polyangiitis | NorLeu3-Angiontensin(1-7)) [NorLeu3-A(1-7)] | Orphan Designation | - |
| malignant carotid body paraganglioma | TXA127 | Orphan Designation | - |
| megacystis-microcolon-intestinal hypoperistalsis syndrome 2 | angiotensin (1-7) | Orphan Designation | - |
| orofaciodigital syndrome I | NorLeu3-Angiontensin(1-7)) [NorLeu3-A(1-7)] | Orphan Designation | - |
| post-treatment Lyme disease syndrome | TXA127 | Orphan Designation | - |
| pulmonary arterial hypertension | Angiotensin-(1-7) | Orphan Designation | - |
| spinal dermal sinus | NorLeu3-Angiotensin(1-7) [NorLeu3-A(1-7)] | Orphan Designation | - |
| treatment-refractory schizophrenia | TXA127 | Orphan Designation | - |