3
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| neuroblastoma | Fenretinide | Orphan Designation | - |
| pediatric hepatocellular carcinoma | Buthionine sulfoxamine | Orphan Designation | - |
| pediatric ovarian dysgerminoma | Buthionine sulfoxamine | Orphan Designation | - |
| pediatric-onset Graves disease | Buthionine sulfoxamine | Orphan Designation | - |