1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| H syndrome | Encapsulated porcine islet preparation | Orphan Designation | - |
| congenital rubella syndrome | Encapsulated porcine islet preparation | Orphan Designation | - |
| diabetes mellitus, permanent neonatal 4 | Encapsulated porcine islet preparation | Orphan Designation | - |