4
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| amyotrophic lateral sclerosis | methylcobalamin | Orphan Designation | - |
| idiopathic neonatal atrial flutter | (-)-Huperzine A | Orphan Designation | - |
| myasthenia gravis | (-)-Huperzine A | Orphan Designation | - |
| neonatal antiphospholipid syndrome | (-)-Huperzine A | Orphan Designation | - |
| pemphigus | afamelanotide | Orphan Designation | - |
| perinatal asphyxia | (-)-Huperzine A | Orphan Designation | - |