4
Orphan Designations
1
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| neuroblastoma | DANYELZANivatrotamab131-I-8H9 monoclonal antibodyMV-NB-02, its bivalent ganglioside vaccine consisting of GD2-lactone and GD3-lactone each covalently conjugated to keyhole hemocyaninDANYELZA® | Orphan Designation | FDA Approved |
| pediatric acute-onset neuropsychiatric syndrome | DANYELZA® | Orphan Designation | - |
| pediatric hepatocellular carcinoma | DANYELZA® | Orphan Designation | - |
| pediatric ovarian dysgerminoma | DANYELZA® | Orphan Designation | - |
| pediatric ovarian germ cell tumor | DANYELZA® | Orphan Designation | - |
| pediatric-onset Graves disease | DANYELZA® | Orphan Designation | - |