2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Kabuki syndrome 1 | dasiglucagon | Orphan Designation | - |
| chronic primary adrenal insufficiency | dasiglucagon | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 9 | dasiglucagon | Orphan Designation | - |
| short bowel syndrome | glepaglutide | Orphan Designation | - |