1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| dermatomyositis | small molecule (heterocyclic compound) that epigenetically regulates gene expression through bromodomain and extra-terminal domain inhibition | Orphan Designation | - |
| mevalonic aciduria | small molecule (heterocyclic compound) that epigenetically regulates gene expression through bromodomain and extra-terminal domain inhibition | Orphan Designation | - |
| nut midline carcinoma | small molecule (heterocyclic compound) that epigenetically regulates gene expression through bromodomain and extra-terminal domain inhibition | Orphan Designation | - |