1
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| heterotaxy, visceral, 1, X-linked | Farydak | Orphan Designation | - |
| mucopolysaccharidosis-plus syndrome | Farydak | Orphan Designation | - |
| multiple congenital anomalies-hypotonia-seizures syndrome 2 | Farydak | Orphan Designation | - |
| plasma cell myeloma | Farydak | Orphan Designation | - |