8
Orphan Designations
0
FDA Approvals
14
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| AIDS | 3'-azido-2',3'dideoxyuridineInterferon beta, recombinant human | Orphan Designation | - |
| B-cell chronic lymphocytic leukemia | Fludara | Orphan Designation | - |
| CREST syndrome | Iloprost solution for infusion | Orphan Designation | - |
| LIPE-related familial partial lipodystrophy | Betapace | Orphan Designation | - |
| Larsen-like osseous dysplasia-short stature syndrome | Betapace | Orphan Designation | - |
| Nager acrofacial dysostosis | Fludarabine phosphate | Orphan Designation | - |
| Proteus-like syndrome | Betapace | Orphan Designation | - |
| Raynaud disease | Iloprost solution for infusion | Orphan Designation | - |
| Weaver syndrome | Fludarabine phosphate | Orphan Designation | - |
| gastrointestinal stromal tumor | Betapace | Orphan Designation | - |
| heparin-induced thrombocytopenia | Iloprost solution for infusion | Orphan Designation | - |
| lice infestation | Betapace | Orphan Designation | - |
| micrognathia-recurrent infections-behavioral abnormalities-mild intellectual disability syndrome | Fludarabine phosphate | Orphan Designation | - |
| thromboangiitis obliterans | Iloprost solution for infusion | Orphan Designation | - |