1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| congenital herpes simplex virus infection | HSV-1-erasing lentivirus-like particle delivering gRNA-expressing cassette and SpCas9 mRNA | Orphan Designation | - |
| herpes simplex virus gingivostomatitis | HSV-1-erasing lentivirus-like particle delivering gRNA-expressing cassette and SpCas9 mRNA | Orphan Designation | - |
| herpes simplex virus keratitis | HSV-1-erasing lentivirus-like particle delivering gRNA-expressing cassette and SpCas9 mRNA | Orphan Designation | - |