14
Orphan Designations
0
FDA Approvals
20
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Behcet disease | dusquetidebeclomethasone 17,21-dipropionate | Orphan Designation | - |
| Castleman disease | beclomethasone 17,21-dipropionate | Orphan Designation | - |
| Qazi Markouizos syndrome | ricin vaccine | Orphan Designation | - |
| T-cell non-Hodgkin lymphoma | Hypericin | Orphan Designation | - |
| acute radiation syndrome | L-arginyl-L-isoleucyl-L-valyl-L-prolyl-L-alanine-amide | Orphan Designation | - |
| gastrointestinal stromal tumor | beclomethasone 17,21-dipropionate | Orphan Designation | - |
| gastrointestinal tuberculosis | beclomethasone 17,21-dipropionate | Orphan Designation | - |
| glioma susceptibility 1 | Hypericin | Orphan Designation | - |
| intestinal atresia | beclomethasone dipropionate | Orphan Designation | - |
| intestinal failure–associated liver disease | beclomethasone dipropionate | Orphan Designation | - |
| intestinal neoplasm | beclomethasone dipropionate | Orphan Designation | - |
| macrophage activation syndrome | dusquetide | Orphan Designation | - |
| pediatric hepatocellular carcinoma | beclomethasone 17,21-diproprionate | Orphan Designation | - |
| pediatric ovarian dysgerminoma | beclomethasone 17,21-diproprionate | Orphan Designation | - |
| pediatric-onset Graves disease | beclomethasone 17,21-diproprionate | Orphan Designation | - |
| post-thrombotic syndrome | subunit protein vaccine of recombinantly expressed Sudan Ebola virus glycoprotein | Orphan Designation | - |
| post-traumatic stress disorder | subunit protein vaccine of recombinantly expressed Sudan Ebola virus glycoprotein | Orphan Designation | - |
| post-vaccinal encephalitis | subunit protein vaccine of recombinantly expressed Sudan Ebola virus glycoprotein | Orphan Designation | - |
| primary cutaneous T-cell non-Hodgkin lymphoma | hypericin | Orphan Designation | - |
| ricin poisoning | ricin vaccine | Orphan Designation | - |