7
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Huntington disease | fasudil HCL | Orphan Designation | - |
| Huntington disease-like 1 | fasudil HCL | Orphan Designation | - |
| Huntington disease-like 2 | fasudil HCL | Orphan Designation | - |
| amyotrophic lateral sclerosis | TrimetazidineFasudil | Orphan Designation | - |
| corticobasal syndrome | Fasudil hydrochloride | Orphan Designation | - |
| frontotemporal dementia | Fasudil | Orphan Designation | - |
| progressive supranuclear palsy | Fasudil | Orphan Designation | - |
| proximal 16p11.2 microdeletion syndrome | Fasudil hydrochloride | Orphan Designation | - |