Comprehensive, easy-to-understand information about this condition
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Kisho delivers this disease record via API, including phenotypes (HPO), genes, orphan drug designations, screening status, and PAG mapping, with version history and governance.
Organizations with orphan designations or approved therapies for this disease
Ambros Therapeutics, Inc.
Other
Axcan Scandipharm Inc.
Other
Beeken, Warren M.D.
Other
Bio-Technology General Corp.
Other
BioMarin Pharmaceutical Inc.
Other
Calliditas Therapeutics AB
Other
Chiron Vision
Other
CuraGen Corporation
Other
Durata Therapeutics International B.V.
Other
Genetix Biotherapeutics Inc.
Other
IC-MedTech Corporation
Other
Kintara Therapeutics, Inc.
Other
Latona Life Sciences, Inc.
Other
Lee’s Pharmaceutical (HK) Limited
Other
Mallinckrodt Hopspital Products
Other
Melville Biologics, Inc.
Other
National Institute of Diabetes, and Digestive and Kidney Diseases
Other
Neuraptive Therapeutics, Inc.
Other
Novartis Pharmaceuticals Corporation
Other
Orphan Europe SARL
Other
PharmaTher Inc.
Other
Prime Medicine
Other
ProQR Therapeutics IV B.V.
Other
Recordati Rare Diseases, Inc.
Other
SmithKline Beecham Pharmaceuticals
Other
Tellus Therapeutics, Inc.
Other
TerSera Therapeutics LLC
Other
Thar Pharma, LLC
Other
X4 Pharmaceuticals, Inc.
Other